Genetic architecture of retinal and macular degenerative diseases: the promise and challenges of next-generation sequencing

R Ratnapriya, A Swaroop - Genome medicine, 2013 - Springer
Inherited retinal degenerative diseases (RDDs) display wide variation in their mode of
inheritance, underlying genetic defects, age of onset, and phenotypic severity. Molecular …

Disruption of the basal body protein POC1B results in autosomal-recessive cone-rod dystrophy

S Roosing, IJC Lamers, E de Vrieze… - The American Journal of …, 2014 - cell.com
Exome sequencing revealed a homozygous missense mutation (c. 317C> G [p. Arg106Pro])
in POC1B, encoding POC1 centriolar protein B, in three siblings with autosomal-recessive …

Biallelic mutations in GNB3 cause a unique form of autosomal-recessive congenital stationary night blindness

A Vincent, I Audo, E Tavares, JT Maynes… - The American Journal of …, 2016 - cell.com
Congenital stationary night blindness (CSNB) is a heterogeneous group of non-progressive
inherited retinal disorders with characteristic electroretinogram (ERG) abnormalities. Riggs …

Whole-exome sequencing identifies KIZ as a ciliary gene associated with autosomal-recessive rod-cone dystrophy

S El Shamieh, M Neuillé, A Terray, E Orhan… - The American Journal of …, 2014 - cell.com
Rod-cone dystrophy (RCD), also known as retinitis pigmentosa, is a progressive inherited
retinal disorder characterized by photoreceptor cell death and genetic heterogeneity …

Substantial restoration of night vision in adult mice with congenital stationary night blindness

J Varin, N Bouzidi, G Gauvain, C Joffrois… - … therapy Methods & …, 2021 - cell.com
Complete congenital stationary night blindness (cCSNB) due to mutations in TRPM1, GRM6,
GPR179, NYX, or leucine-rich repeat immunoglobulin-like transmembrane domain 3 …

[HTML][HTML] Mutations in GRM6 identified in consanguineous Pakistani families with congenital stationary night blindness

MA Naeem, ADH Gottsch, I Ullah, SN Khan… - Molecular …, 2015 - ncbi.nlm.nih.gov
Purpose This study was undertaken to investigate the causal mutations responsible for
autosomal recessive congenital stationary night blindness (CSNB) in consanguineous …