[HTML][HTML] Oligonucleotide Therapies for Facioscapulohumeral Muscular Dystrophy: Current Preclinical Landscape

SL Beck, T Yokota - International Journal of Molecular Sciences, 2024 - mdpi.com
Facioscapulohumeral muscular dystrophy (FSHD) is an inherited myopathy, characterized
by progressive and asymmetric muscle atrophy, primarily affecting muscles of the face …

Temporal variation in p38-mediated regulation of DUX4 in facioscapulohumeral muscular dystrophy

R Vangipurapu, J Oliva, A Fox, FM Sverdrup - Scientific Reports, 2024 - nature.com
Facioscapulohumeral muscular dystrophy (FSHD) is a degenerative muscle disease caused
by loss of epigenetic silencing and ectopic reactivation of the embryonic double homeobox …