Muscle as a target for supplementary factor IX gene transfer
BE Hoffman, E Dobrzynski, L Wang, L Hirao… - Human gene …, 2007 - liebertpub.com
Immune responses to the factor IX (F. IX) transgene product are a concern in gene therapy
for the X-linked bleeding disorder hemophilia B. The risk for such responses is determined …
for the X-linked bleeding disorder hemophilia B. The risk for such responses is determined …