Effective viral-mediated lung gene therapy: is airway surface preparation necessary?

A McCarron, P Cmielewski, V Drysdale, D Parsons… - Gene Therapy, 2023 - nature.com
Gene-based therapeutics are actively being pursued for the treatment of lung diseases.
While promising advances have been made over the last decades, the absence of clinically …

Gene therapy for cystic fibrosis lung disease

SG Sumner-Jones, DR Gill, SC Hyde - Gene Therapy for Autoimmune and …, 2010 - Springer
Cystic fibrosis (CF) is characterised by respiratory and pancreatic deficiencies that stem from
the loss of fully functional CFTR (CF transmembrane conductance regulator) at the …