Polymeric delivery of therapeutic nucleic acids

R Kumar, CF Santa Chalarca, MR Bockman… - Chemical …, 2021 - ACS Publications
The advent of genome editing has transformed the therapeutic landscape for several
debilitating diseases, and the clinical outlook for gene therapeutics has never been more …

Understanding nanomaterial–liver interactions to facilitate the development of safer nanoapplications

J Li, C Chen, T Xia - Advanced Materials, 2022 - Wiley Online Library
Nanomaterials (NMs) are widely used in commercial and medical products, such as
cosmetics, vaccines, and drug carriers. Exposure to NMs via various routes such as dermal …

Polyplex designs for improving the stability and safety of RNA therapeutics

S Uchida, CYJ Lau, M Oba, K Miyata - Advanced Drug Delivery Reviews, 2023 - Elsevier
Nanoparticle-based delivery systems have contributed to the recent clinical success of RNA
therapeutics, including siRNA and mRNA. RNA delivery using polymers has several distinct …

Core polymer optimization of ternary siRNA nanoparticles enhances in vivo safety, pharmacokinetics, and tumor gene silencing

SS Patel, EN Hoogenboezem, F Yu, CR DeJulius… - Biomaterials, 2023 - Elsevier
Gene silencing with siRNA nanoparticles (si-NPs) is promising but still clinically unrealized
for inhibition of tumor driver genes. Ternary si-NPs containing siRNA, a single block NP core …

Therapeutic RNA delivery for COVID and other diseases

C Dobrowolski, K Paunovska, MZC Hatit… - Advanced …, 2021 - Wiley Online Library
RNA can alter the expression of endogenous genes and can be used to express therapeutic
proteins. As a result, RNA‐based therapies have recently mitigated disease in patients. Yet …

Stimulating TAM-mediated anti-tumor immunity with mannose-decorated nanoparticles in ovarian cancer

EB Glass, AA Hoover, KK Bullock, MZ Madden… - BMC cancer, 2022 - Springer
Background Current cancer immunotherapies have made tremendous impacts but generally
lack high response rates, especially in ovarian cancer. New therapies are needed to provide …

Optimizing an Antioxidant TEMPO Copolymer for Reactive Oxygen Species Scavenging and Anti-Inflammatory Effects in Vivo

CR DeJulius, BR Dollinger, TE Kavanaugh… - Bioconjugate …, 2021 - ACS Publications
Oxidative stress is broadly implicated in chronic, inflammatory diseases because it causes
protein and lipid damage, cell death, and stimulation of inflammatory signaling …

PEGylated polyester nanoparticles trigger adverse events in a large animal model of Trauma and in Naı̈ve animals: understanding Cytokine and Cellular …

N Maisha, C Kulkarni, N Pandala, R Zilberberg… - ACS …, 2022 - ACS Publications
Intravenously infusible nanoparticles to control bleeding have shown promise in rodents, but
translation into preclinical models has been challenging as many of these nanoparticle …

Structural optimization of siRNA conjugates for albumin binding achieves effective MCL1-directed cancer therapy

EN Hoogenboezem, SS Patel, JH Lo… - Nature …, 2024 - nature.com
The high potential of siRNAs to silence oncogenic drivers remains largely untapped due to
the challenges of tumor cell delivery. Here, divalent lipid-conjugated siRNAs are optimized …

Replacement of L-amino acid peptides with D-amino acid peptides mitigates anti-PEG antibody generation against polymer-peptide conjugates in mice

M Sylvestre, S Lv, LF Yang, N Luera, DJ Peeler… - Journal of Controlled …, 2021 - Elsevier
The generation of anti-PEG antibodies in response to PEGylated proteins, peptides, and
carriers significantly limits their clinical applicability. IgM antibodies mediate the clearance of …