A Step-By-Step Method to Detect Neutralizing Antibodies Against AAV using a Colorimetric Cell-Based Assay

S Bass-Stringer, CJ Thomas, CN May… - JoVE (Journal of …, 2021 - jove.com
Recombinant adeno-associated viruses (rAAV) have proven to be a safe and successful
vector for transferring genetic material to treat various health conditions in both the …

Predicting the Impact of Dialyzer Choice and Binder Dialysate Flow Rate on Bilirubin Removal

A Novokhodko, N Du, S Hao, Z Wang, Z Shu, S Ahmad… - bioRxiv, 2024 - biorxiv.org
Liver failure is the 12th leading cause of death worldwide. Protein bound toxins such as
bilirubin are responsible for many complications of the disease. Binder dialysis systems use …

Gene Replacement Therapy for Duchenne Muscular Dystrophy

K Hollinger, JM Crudele, JS Chamberlain - Muscle Gene Therapy, 2019 - Springer
Duchenne muscular dystrophy (DMD) is a fatal, X-linked disease caused by mutations in the
massive dystrophin gene that lead to extremely low or non-detectable levels of dystrophin …