Current avenues of gene therapy in Pompe disease
C Leon-Astudillo, PD Trivedi, RC Sun… - Current Opinion in …, 2023 - journals.lww.com
Gene therapy for the treatment of patients with Pompe disease is feasible and offers an
opportunity to fully correct the principal pathology leading to cellular glycogen accumulation …
opportunity to fully correct the principal pathology leading to cellular glycogen accumulation …
Characterization of the human blood virome in Iranian multiple transfused patients
M Thijssen, G Khamisipour, M Maleki, T Devos, G Li… - Viruses, 2023 - mdpi.com
Blood transfusion safety is an essential element of public health. Current blood screening
strategies rely on targeted techniques that could miss unknown or unexpected pathogens …
strategies rely on targeted techniques that could miss unknown or unexpected pathogens …
[PDF][PDF] A mechanistic view on the genome replication mechanisms of Adeno-associated Virus Type 2
S Marti - 2023 - zora.uzh.ch
Adeno-associated Virus (AAV) depends on helper factors for productive replication. Upon
cell entry, it is thought to replicate its DNA through either the rolling circle or rolling hairpin …
cell entry, it is thought to replicate its DNA through either the rolling circle or rolling hairpin …