CRISPR/Cas9-generated mouse model with humanizing single-base substitution in the Gnao1 for safety studies of RNA therapeutics
AV Polikarpova, TV Egorova, EA Lunev… - Frontiers in Genome …, 2023 - frontiersin.org
The development of personalized medicine for genetic diseases requires preclinical testing
in the appropriate animal models. GNAO1 encephalopathy is a severe neurodevelopmental …
in the appropriate animal models. GNAO1 encephalopathy is a severe neurodevelopmental …