Gene Therapy for β-Hemoglobinopathies: From Discovery to Clinical Trials

EER Segura, PG Ayoub, KL Hart, DB Kohn - Viruses, 2023 - mdpi.com
Investigations to understand the function and control of the globin genes have led to some of
the most exciting molecular discoveries and biomedical breakthroughs of the 20th and 21st …