Corticosteroids for the treatment of Duchenne muscular dystrophy

E Matthews, R Brassington, T Kuntzer… - Cochrane Database …, 2016 - cochranelibrary.com
Background Duchenne muscular dystrophy (DMD) is the most common muscular dystrophy
of childhood. Untreated, this incurable disease, which has an X‐linked recessive …

Diagnosis and management of Duchenne muscular dystrophy, part 1: diagnosis, and pharmacological and psychosocial management

K Bushby, R Finkel, DJ Birnkrant, LE Case… - The Lancet …, 2010 - thelancet.com
Duchenne muscular dystrophy (DMD) is a severe, progressive disease that affects 1 in 3600–
6000 live male births. Although guidelines are available for various aspects of DMD …

Diagnosis and management of Duchenne muscular dystrophy, part 2: implementation of multidisciplinary care

K Bushby, R Finkel, DJ Birnkrant, LE Case… - The Lancet …, 2010 - thelancet.com
Optimum management of Duchenne muscular dystrophy (DMD) requires a multidisciplinary
approach that focuses on anticipatory and preventive measures as well as active …

Standard of care versus new-wave corticosteroids in the treatment of Duchenne muscular dystrophy: Can we do better?

S Kourakis, CA Timpani, DG Campelj, P Hafner… - Orphanet Journal of …, 2021 - Springer
Background Pharmacological corticosteroid therapy is the standard of care in Duchenne
Muscular Dystrophy (DMD) that aims to control symptoms and slow disease progression …

Orthopedic outcomes of long-term daily corticosteroid treatment in Duchenne muscular dystrophy

WM King, R Ruttencutter, HN Nagaraja, V Matkovic… - Neurology, 2007 - AAN Enterprises
Objective: To document the effects of long-term daily corticosteroid treatment on a variety of
orthopedic outcomes in boys with Duchenne muscular dystrophy. Methods: We reviewed the …

The role of corticosteroids in muscular dystrophy: a critical appraisal

C Angelini - Muscle & Nerve: Official Journal of the American …, 2007 - Wiley Online Library
Over the years various steroid trials have been conducted in Duchenne muscular dystrophy
(DMD). In children who are still able to walk as well as in those who are wheelchair‐bound …

Official positions of the International Society for Clinical Densitometry (ISCD) on DXA evaluation in children and adolescents

ML Bianchi, S Baim, NJ Bishop, CM Gordon… - Pediatric …, 2010 - Springer
Dual-energy X-ray absorptiometry (DXA) is the most widely used technical instrument for
evaluating bone mineral content (BMC) and density (BMD) in patients of all ages. However …

Mechanisms inducing low bone density in Duchenne muscular dystrophy in mice and humans

A Rufo, A Del Fattore, M Capulli… - Journal of Bone and …, 2011 - academic.oup.com
Patients affected by Duchenne muscular dystrophy (DMD) and dystrophic MDX mice were
investigated in this study for their bone phenotype and systemic regulators of bone turnover …

Report on the 124th ENMC International Workshop. Treatment of Duchenne muscular dystrophy; defining the gold standards of management in the use of …

K Bushby, F Muntoni, A Urtizberea, R Hughes… - Neuromuscular …, 2004 - Elsevier
Thirty-two participants representing parents, funding agencies and clinicians involved in the
care of children with Duchenne Muscular Dystrophy (DMD) from Belgium, Canada …

Rehabilitation management of the patient with Duchenne muscular dystrophy

LE Case, SD Apkon, M Eagle, A Gulyas, L Juel… - …, 2018 - publications.aap.org
Steadily improving management of Duchenne muscular dystrophy (DMD) continues to lead
to improved physical and functional status, allowing increasingly successful transitions to …