Thalassaemia
A Kattamis, JL Kwiatkowski, Y Aydinok - The lancet, 2022 - thelancet.com
Thalassaemia is a diverse group of genetic disorders with a worldwide distribution affecting
globin chain synthesis. The pathogenesis of thalassaemia lies in the unbalanced globin …
globin chain synthesis. The pathogenesis of thalassaemia lies in the unbalanced globin …
Gene therapy and editing in the treatment of hereditary blood disorders: Medical and ethical aspects
P Cano Alburquerque, L Gómez-Tatay… - Clinical …, 2022 - journals.sagepub.com
Gene therapy and gene editing are revolutionising the treatment of genetic diseases, most
notably haematological disorders. This paper evaluates the use of both techniques in …
notably haematological disorders. This paper evaluates the use of both techniques in …