Myhre syndrome in adulthood: clinical variability and emerging genotype-phenotype correlations

E Vanbelleghem, T Van Damme, A Beyens… - European Journal of …, 2024 - nature.com
Abstract Myhre syndrome (MS, MIM 139210) is a rare multisystemic disorder caused by
recurrent pathogenic missense variants in SMAD4. The clinical features have been mainly …

DNA methylation profiling in Kabuki syndrome: reclassification of germline KMT2D VUS and sensitivity in validating postzygotic mosaicism

M Niceta, A Ciolfi, M Ferilli, L Pedace… - European Journal of …, 2024 - nature.com
Autosomal dominant Kabuki syndrome (KS) is a rare multiple congenital anomalies/
neurodevelopmental disorder caused by heterozygous inactivating variants or structural …

Sex-specific difference in phenotype of Kabuki syndrome type 2 patients: a matched case-control study

Y Wang, Y Xu, Y Chen, Y Hu, Q Li, S Liu, J Wang… - BMC pediatrics, 2024 - Springer
Background Kabuki syndrome (KS) is a monogenic disorder leading to special facial
features, mental retardation, and multiple system malformations. Lysine demethylase …

A Case of Kabuki Syndrome Caused by a Novel Mutation in KMT2D and a Literature Review of Ocular Abnormalities

Y Zhang, X Chen, L Ye - 2024 - researchsquare.com
Objective: By summarizing the clinical characteristics and genetic variations, this study aims
to report a case of one child with type I Kabuki syndrome (KS), and to analyze the features …