Targeted delivery of acid alpha-glucosidase corrects skeletal muscle phenotypes in Pompe disease mice

AD Baik, PT Calafati, NA Aaron, A Mehra… - bioRxiv, 2020 - biorxiv.org
Lysosomal diseases are a class of genetic disorders predominantly caused by loss of
lysosomal hydrolases, leading to lysosomal and cellular dysfunction. Enzyme Replacement …

[PDF][PDF] Targeted delivery of acid alpha-glucosidase corrects skeletal muscle phenotypes in Pompe disease mice

AD Baik, PT Calafati, NA Aaron, A Mehra, LM Tank… - scholar.archive.org
Lysosomal diseases are a class of genetic disorders predominantly caused by loss of
lysosomal hydrolases, leading to lysosomal and cellular dysfunction. Enzyme Replacement …

[PDF][PDF] Targeted delivery of acid alpha-glucosidase corrects skeletal muscle phenotypes in Pompe disease mice

AD Baik, PT Calafati, NA Aaron, A Mehra, LM Tank… - researchgate.net
Lysosomal diseases are a class of genetic disorders predominantly caused by loss of
lysosomal hydrolases, leading to lysosomal and cellular dysfunction. Enzyme Replacement …

Targeted delivery of acid alpha-glucosidase corrects skeletal muscle phenotypes in Pompe disease mice

AD Baik, PT Calafati, NA Aaron, A Mehra… - 2020 - europepmc.org
Lysosomal diseases are a class of genetic disorders predominantly caused by loss of
lysosomal hydrolases, leading to lysosomal and cellular dysfunction. Enzyme Replacement …

[PDF][PDF] Targeted delivery of acid alpha-glucosidase corrects skeletal muscle phenotypes in Pompe disease mice

AD Baik, PT Calafati, NA Aaron, A Mehra, LM Tank… - academia.edu
Lysosomal diseases are a class of genetic disorders predominantly caused by loss of
lysosomal hydrolases, leading to lysosomal and cellular dysfunction. Enzyme Replacement …